HSA Isoform Profile as Biomarker of Chronic Liver Disease Staging

Biomarker description

  • Target: Panel of 10 circulating HSA isoforms; multivariate spectral fingerprint (66,000–68,000 Da)
  • Disease context: Liver fibrosis / Chronic Liver Disease (CLD) — staging F0/F1 through F4_C
  • Analytical method: Top-down LC-MS (LC-HR-MS); absolute quantification (g/L) via internal calibration
  • Source study: el-balkhi-2025 — El Balkhi et al. 2025 (ALBOM study)

Biomarker panel — 10 isoforms

The 10 quantified isoforms

IsoformPTM(s)Δmass (Da)Pattern with CLD progression
Native HSA0↓ progressive; precipitous F4_B/C
HSA-DAN-term truncation−115↓ all stages (paradoxically lower in patients)
HSA-LC-term truncationvariableNo significant change
HSA+CYSCysteinylation Cys34+119Biphasic — peaks F4_A (11.1 g/L), falls F4_B/C
HSA+SO₃HSulfonylation Cys34+48↓ F4_B/C
HSA+GLYCGlycation (mono)+162Biphasic — peaks F3, falls F4_B/C
HSA-DA+CYSTruncation + CYS−115 +119↓ F4_B/C
HSA+CYS+GLYCCYS + glycation+281Biphasic — peaks F3 (1.9 g/L)
HSA+2GLYCDouble glycation+324Biphasic — peaks F4_A
HSA+CYS+2GLYCCYS + 2× glycation+443Progressive ↑ — end-stage marker

The three patterns (biological interpretation)

  1. Decrease group: Reflects loss of hepatocyte synthetic capacity and depletion of functional HSA substrate (native, truncated, irreversibly-oxidized forms all reduced in advanced disease)
  2. Biphasic group: Reflects escalating oxidative/glycative stress in compensated disease followed by exhaustion of the substrate pool in decompensation. Absolute ↓ but ratio-to-native ↑ — the ratio is the correct metric
  3. Increase group: HSA+CYS+2GLYC — cumulative end-stage damage marker; measures the proportion of HSA that has undergone maximal modification; near-zero in healthy individuals

Clinical performance

Native HSA (single marker)

ComparisonAUC
Controls vs F0/F10.67
Controls vs F4_B0.99
Controls vs F4_C0.89

Best for decompensated cirrhosis; limited for early fibrosis.

Isoform ratios (normalized to native HSA)

RatioComparisonSensitivitySpecificity
HSA+CYS/NativeControls vs F4_C65%99%
HSA+GLYC/NativeControls vs F2detects earliest ←
HSA+GLYC/NativeControls vs F4_B85%100%
HSA+GLYC/NativeControls vs F4_C70%99%
HSA+CYS+GLYC/NativeControls vs F4_B77%99%
HSA+CYS+GLYC/NativeControls vs F4_C70%99%

HSA+GLYC/Native is the best single-ratio discriminator; also uniquely capable of discriminating controls from F2 (early disease).

Multivariate OrdinalForest model (75 spectral features + 4 clinical variables)

Platformn_testQWK95% CIAccuracy (3-class)
Bruker timsTOF Pro2460.8620.735–0.92381.5%
Sciex TripleTOF 5600+490.9160.822–0.964
FIB-4 index (comparator)same0.188–0.22959.3%

Improvement over FIB-4: +26 percentage points accuracy. FIB-4 gray zone (1.30–2.67): ALBOM correctly classifies 62.5% (⚠️ n=8, preliminary).

Cross-platform reproducibility

  • McNemar’s test: p = 0.149 → not significantly different between Bruker and Sciex
  • Jaccard index of errors: 0.696 → errors are biologically driven (boundary stages), not instrument artifacts
  • Both platforms: QWK within “substantial to near-perfect agreement” range

Validation status

  • ☑ Discovery — el-balkhi-2025 (published, Scientific Reports 2026, DOI 10.1038/s41598-026-57614-y)
  • ☑ Cross-instrument reproducibility (within single center)
  • ☐ Replicated (independent cohort)
  • ◧ Externally validated (multicenter) — MALAHBAR ongoing: 560 patients / 8 French CHUs (target >700), readout expected 2027
  • ◧ Prospective longitudinal validation (MALAHBAR NCT06318949)
  • ☐ Clinically approved

Advantages over existing markers

FeatureFIB-4ElastographyHSA isoform profile
InvasiveNoNoNo
Multi-class stagingWeakWeakYes (6 classes)
Gray zone problemSevere (30–40%)ModerateReduced (62.5% classified)
Biological insightIndirectStructural proxyDirect molecular readout
Etiology-specificNoNo⚠️ To be established
Platform portabilityUniversalDevice-specificCross-manufacturer confirmed
Clinical deploymentImmediateModerate barrierHigh barrier (LC-HR-MS)

HSA isoforms provide a functional and molecular measure of CLD severity rather than anatomical or enzymatic surrogates.

The biphasic paradox — key interpretive concept

Modified isoforms (HSA+CYS, HSA+GLYC) peak in absolute concentration at compensated cirrhosis (F4_A), then fall in decompensation (F4_B/C). This can be mistaken for improvement. The correct interpretation:

  • Absolute ↓ = substrate (native HSA) depleted faster than modification accrues
  • Ratio (isoform/native) ↑ = the proportion of damaged albumin continues to rise
  • Always use ratios, not absolute values, for diagnostic interpretation

Limitations and gaps

  • ⚠️ Single-center cross-sectional cohort (n=254 total) — limited generalizability
  • ⚠️ Etiology bias: MASH + ALD predominate; etiology-specific profiles not yet characterized
  • ⚠️ F2/F3 overlap: FibroScan staging limitations cause cluster dispersion; biopsy validation limited
  • ⚠️ Platform 1 (Bruker): baseline correction attenuates high-mass glycated species >67,500 Da — Platform 1 classifier is valid but sub-optimal for poly-glycated endpoints
  • ⚠️ Gray zone FIB-4 analysis: n=8, hypothesis-generating only
  • ⚠️ LC-HR-MS not universally available in routine clinical labs

Our contribution

This biomarker page documents the primary output of the ALBOM study, generated using the CQFD-PTM pipeline and Top-down proteomics methodology developed at CHU Limoges / INSERM UMR1248. The ALBOM study is the proof-of-concept clinical validation for both the pipeline and the biomarker concept.

Key studies

  • el-balkhi-2025 — El Balkhi & Berrah et al. 2025 (ALBOM manuscript, Scientific Reports submission)